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789
大部分患病儿童的免疫系统回复正常。
来自美国两间医疗中心的医生,近日成功将艾滋病病毒(HIV)化成基因治疗工具,成功令10名患上俗称“泡泡男孩病”、即严重联合免疫缺陷病(SCID)儿童的免疫系统回复正常。有关研究已于周四刊于美国的《新英格兰医学杂志》内。
美国的圣祖德儿童研究医院联同加州大学旗下的儿童医院,先从儿童抽取骨髓,并使用一种经改良、不会致病的HIV植入患者缺乏的基因,然而注入患者细胞,从而使蛋白质构建正常运作的免疫系统。
报道指,几乎所有患者于接受治疗三个月后,都出现无缺陷的免疫细胞,现时发育正常,与免疫系统受损有关的感染均已消失,亦没有患上白血病的迹象。
领导是次研究的马姆恰日表示:“孩子们能够得到治疗,是因为我们首次能够回复三种类型的细胞,构成一个完整的免疫系统。我们的病人能够产生一个健康、功能齐全的免疫系统,现在对疫苗亦有反应,是基因治疗试验的第一次。”
“泡泡男孩病”是罕见遗传病,患者因基因问题而几乎没有免疫能力,需在无菌的情况下生活。
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